RARECast

548 Episodio

1. Deriving Rare Disease Therapies from Human Plasma

   Pubblicato: 18/10/2017
2. Learning to Live with Purpose

   Pubblicato: 11/10/2017
3. A Mother's Race to Find a Treatment for Her Daughter's Ultra-Rare Condition

   Pubblicato: 04/10/2017
4. Screening for Rare Diseases

   Pubblicato: 27/09/2017
5. A Look at the Changing World of Work for People with a Chronic Illness

   Pubblicato: 20/09/2017
6. Aligning Interests in Rare Disease Partnerships

   Pubblicato: 13/09/2017
7. A Veteran Venture Capitalist Discusses Investing in Rare Disease Drug Development

   Pubblicato: 06/09/2017
8. A Patient Group Crafts Guidelines for Working with Pharma

   Pubblicato: 30/08/2017
9. Bringing Innovation to Business Models for Rare Disease Drug Development

   Pubblicato: 23/08/2017
10. Rethinking Accessibility and Dependency

    Pubblicato: 16/08/2017
11. How Simon Wheatcroft, Blinded by a Rare Disease, Became an Ultramarathoner

    Pubblicato: 09/08/2017
12. Spark Hoping Its Luxturna Will Become First FDA-Approved Gene Therapy

    Pubblicato: 02/08/2017
13. What Rare Patient-Investors Can Learn From Venture Capitalists

    Pubblicato: 26/07/2017
14. Novel Effort Delivers Failed DMD Drug to Former Clinical Trial Participants

    Pubblicato: 19/07/2017
15. Centogene Seeks to Deliver Diagnoses to Rare Disease Patients Early

    Pubblicato: 12/07/2017
16. Albireo Advances Pipeline for Rare Liver and Gastrointestinal Diseases

    Pubblicato: 05/07/2017
17. aTyr Pharma Seeks to Modulate Activity in FSHD and Other Rare Disease

    Pubblicato: 28/06/2017
18. Summit Pursues A Different Approach to Treating Duchenne

    Pubblicato: 21/06/2017
19. Delivering Enzyme Replacement Therapies Across the Blood-Brain Barrier

    Pubblicato: 14/06/2017
20. Sangamo Advances Gene Editing Therapies for Multiple Rare Diseases into the Clinic

    Pubblicato: 07/06/2017