RARECast

548 Episodio

1. Addressing the Challenges of Rare Disease Drug Development

   Pubblicato: 07/03/2018
2. Giving Voice to Patients at the FDA

   Pubblicato: 28/02/2018
3. Finding a Rare Friend

   Pubblicato: 21/02/2018
4. Why a Sports Physical May Trigger a Doctor to Think About a Rare Diagnosis

   Pubblicato: 14/02/2018
5. UPenn's Orphan Disease Center Takes a Rare Approach

   Pubblicato: 07/02/2018
6. How Patients Can Accelerate Translational Research in Rare Disease

   Pubblicato: 31/01/2018
7. Notre Dame Center Leverages Commonalities of Rare and Neglected Diseases

   Pubblicato: 24/01/2018
8. GalXC Quest: Dicerna Bets on Its Unqiue Approach to RNAi

   Pubblicato: 17/01/2018
9. Pharnext Takes a Unique Twist on Repurposing Drugs for Rare Diseases

   Pubblicato: 10/01/2018
10. uniQure Seeks to Find Elusive Market Success with Hemophilia B Gene Therapy

    Pubblicato: 03/01/2018
11. Savara Advances Pipeline of Inhaled Therapeutics for Rare Lung Diseases

    Pubblicato: 27/12/2017
12. Why the Microbiome May Provide a Novel Approach to Treating Certain Rare Diseases

    Pubblicato: 20/12/2017
13. FDA Outlines a Collaborative Approach for Pediatric Rare Disease Trials

    Pubblicato: 13/12/2017
14. Why Patient-Centred Outcomes Are Critical to Rare Disease Drug Trials

    Pubblicato: 06/12/2017
15. What the FDA's New Framework Means for Regenerative Therapies

    Pubblicato: 29/11/2017
16. Measuring the Value of Therapies for Ultra-Rare Diseases

    Pubblicato: 22/11/2017
17. Lessons from Pitching Venture Capitalists

    Pubblicato: 15/11/2017
18. Health Canada Scraps Plans for Orphan Drug Framework

    Pubblicato: 08/11/2017
19. New Investment Boosts Rare Disease Drug Accelerator

    Pubblicato: 01/11/2017
20. Understanding Rare Disease Caregiver Needs

    Pubblicato: 25/10/2017