RARECast

548 Episodio

1. Forging a Research Agenda for a Rare Disease

   Pubblicato: 25/07/2018
2. Making the Journey from All-American Athlete to Rare Disease Advocate

   Pubblicato: 18/07/2018
3. How Destiny Lamonte Learned to Advocate for Herself and Others

   Pubblicato: 11/07/2018
4. Where the NIH Does Its Banking

   Pubblicato: 05/07/2018
5. Making Sense of Nonsense Mutations

   Pubblicato: 27/06/2018
6. Rewriting Faulty RNA

   Pubblicato: 20/06/2018
7. Experimental Drug for "Elephant Man" Disease May Benefit Certain Cancers Too

   Pubblicato: 13/06/2018
8. Programming Stem Cells to Protect Neurons in ALS and other Neurodegenerative Conditions

   Pubblicato: 06/06/2018
9. Why a Topical, Off-the-Shelf, Gene Therapy May Hold Promise for a Rare Skin Condition

   Pubblicato: 30/05/2018
10. An Ironman Champion with Cystic Fibrosis Discusses her Changing Relationship with Her Disease

    Pubblicato: 23/05/2018
11. Why an Experimental Fragile X Drug May Treat a Range of Neurodegenerative Diseases

    Pubblicato: 16/05/2018
12. The Case for a Daily Self-Injection to Treat Hemophilia

    Pubblicato: 09/05/2018
13. Addressing the Challenges of R&D for Rare Cancer Therapies

    Pubblicato: 02/05/2018
14. Learning to Communicate and Collaborate as a Patient Advocate

    Pubblicato: 25/04/2018
15. Seeking Answers for Undiagnosed Patients

    Pubblicato: 18/04/2018
16. When "Undiagnosed" Is Your Diagnosis

    Pubblicato: 11/04/2018
17. The Decision to Get Tested for Huntington's Disease and How It Changed Seth Rotberg's Life

    Pubblicato: 04/04/2018
18. Nonprofit Sees Need in Developing Gene Therapies for Inherited Eye Disesases

    Pubblicato: 29/03/2018
19. Casting a Wider Net for Genetic Diseases

    Pubblicato: 21/03/2018
20. Corbus Seeks to Quiet the Immune System in Chronic Conditions

    Pubblicato: 14/03/2018