RARECast

548 Episodio

1. Navigating the Challenges of Rare Disease Drug Development

   Pubblicato: 31/05/2017
2. Accelerating Rare Disease Drug Discovery

   Pubblicato: 24/05/2017
3. Experimental Rare Disease Therapy Wins New FDA Reg Med Designation

   Pubblicato: 17/05/2017
4. How Rare Disease Patients Can Get their Voices Heard in Drug Discovery and Development

   Pubblicato: 10/05/2017
5. One Patient's Difficult Road to a Rare Diagnosis

   Pubblicato: 03/05/2017
6. How Researchers Diagnosed Four Patients with a Never-Before-Identified Rare Disease in a Day

   Pubblicato: 26/04/2017
7. Stem Cell Gene Therapy Restores Immune System in Kids with SCID

   Pubblicato: 19/04/2017
8. Rare Disease Advocates Push for Incentives to Drugmakers Pulled from Cures Act

   Pubblicato: 12/04/2017
9. Non-Profit Drug Company Seeks to Advance Rare Disease Therapies

   Pubblicato: 05/04/2017
10. Innovative Collaboration Model Drives Treatment for Rare Disease

    Pubblicato: 29/03/2017
11. Girl with Rare Disease Inspires Search for Bone Marrow Donors

    Pubblicato: 22/03/2017
12. A Quest for Tribe: Searching for Others with the Same Ultra-Rare Mutation

    Pubblicato: 15/03/2017
13. Raising Awareness in a Town with a History of a Rare Disease

    Pubblicato: 08/03/2017
14. Helping Rare Disease Patients Navigate the World of Information

    Pubblicato: 01/03/2017
15. Overcoming the Challenges of Rare Disease Drug Development

    Pubblicato: 22/02/2017
16. Moving Rare Disease Therapies from Hope to Reality

    Pubblicato: 15/02/2017
17. Children’s National Launches First-of-its-Kind Rare Disease Center

    Pubblicato: 08/02/2017
18. A Common Link in a Group of Rare Diseases Creates an Opportunity for Repurposing

    Pubblicato: 01/02/2017
19. Sobi Works to Expand Rare Disease Indications for Its Drugs

    Pubblicato: 25/01/2017
20. Why Rare Disease Patients Should Work Together to Address Common Concerns

    Pubblicato: 18/01/2017