RARECast

548 Episodio

1. Choosing the Right Viral Vector for a Gene Therapy

   Pubblicato: 01/04/2021
2. A Software Platform to Give Patients the Tools to Build Treatments for Rare Genetic Diseases

   Pubblicato: 25/03/2021
3. Side Effects: The Toll a Rare Disease Can Take on a Family in Pursuit of a Cure

   Pubblicato: 19/03/2021
4. Realizing the Potential of CRISPR Gene Editing

   Pubblicato: 12/03/2021
5. Understanding the Economic Toll of Rare Disease in the United States

   Pubblicato: 04/03/2021
6. The Promise of Gene-Based Therapies for Neurodegenerative Conditions

   Pubblicato: 25/02/2021
7. Moving Beyond Viral Vectors for Gene Therapies

   Pubblicato: 19/02/2021
8. Acquisitions Help Jazz Build Toward Commercial Crescendo

   Pubblicato: 12/02/2021
9. Powerful Gene Editing Approach Offers the Promise of Correcting a Range of Rare Diseases

   Pubblicato: 05/02/2021
10. A Child's-Eye-View of Clinical Trials

    Pubblicato: 29/01/2021
11. Using Nanoliposomes to Make Cancer Therapies Safer and More Effective

    Pubblicato: 21/01/2021
12. Accelerating Treatments for Rare Disease through Data Sharing

    Pubblicato: 14/01/2021
13. Treating the Root Cause of Sickle Cell Disease

    Pubblicato: 08/01/2021
14. Targeting a Common Pathway in Genetic Forms of Obesity

    Pubblicato: 30/12/2020
15. After Pruning Orchard, Gaspar Focuses on High Value Opportunities

    Pubblicato: 23/12/2020
16. Writing a New Chapter of Genetic Medicine

    Pubblicato: 17/12/2020
17. How an Ultra-Rare Disease Patient Organization Drove Research to a Treatment

    Pubblicato: 10/12/2020
18. With a New Identity, Travere Thearpeutics Seeks to Find Its True Path

    Pubblicato: 04/12/2020
19. Making Gene Therapies Accessible to Patient with Ultra-Rare Conditions

    Pubblicato: 26/11/2020
20. Using RNA Therapies to Target Inherited Retinal Diseases

    Pubblicato: 20/11/2020