RARECast

548 Episodio

1. Addressing the Delivery Challenges of Genetic Medicines

   Pubblicato: 19/08/2021
2. Targeting Tissues Throughout the Body with RNA Therapies

   Pubblicato: 12/08/2021
3. Delivering Rare Disease Therapies to Patients in Need

   Pubblicato: 05/08/2021
4. An Advocate's Journey through Diagnosis, Loss, and Hope

   Pubblicato: 29/07/2021
5. Using Model Systems to Find Drugs to Repurpose for Rare Diseases

   Pubblicato: 22/07/2021
6. How a Small and Young Foundation Catalyzed Research into a Rare Disease

   Pubblicato: 16/07/2021
7. Overcoming the Limitations of Conventional Cell Engineering

   Pubblicato: 08/07/2021
8. Experimental Therapy for Rare Endocrine Disorder Offers Hope of Improved Care

   Pubblicato: 02/07/2021
9. Forging Gene Therapy Capacity and a Pipeline at the Same Time

   Pubblicato: 24/06/2021
10. Using A Natural DNA Repair Process to Improve Genetic Medicines

    Pubblicato: 18/06/2021
11. Empowering Rare Disease Patients with their Own Health Records

    Pubblicato: 10/06/2021
12. Targeting CNS Disease with Gene Therapies

    Pubblicato: 03/06/2021
13. A New Therapy Offers A Different Approach to Inhibiting the Complement System

    Pubblicato: 28/05/2021
14. Bringing Aberrant Proteins Back into the Fold

    Pubblicato: 20/05/2021
15. A Cat who Curates Rare Mice

    Pubblicato: 13/05/2021
16. Putting the Patient at the Center of Rare Disease Clinical Trials

    Pubblicato: 06/05/2021
17. Creating a Toolkit to Accelerate the Development of Gene Editing Therapies

    Pubblicato: 29/04/2021
18. PTC Looks to Advanced Therapies

    Pubblicato: 22/04/2021
19. Going to Extreme Lengths

    Pubblicato: 15/04/2021
20. Everything’s up to Date in Kansas City, at Least When It Comes to Genomics

    Pubblicato: 08/04/2021