RARECast

548 Episodio

1. Part 4-Gene Therapy: A Researcher’s Perspective

   Pubblicato: 13/11/2020
2. Part 3-Gene Therapy: An Industry Perspective

   Pubblicato: 06/11/2020
3. Part 2-Gene Therapy: A Patient Advocate's Perspective

   Pubblicato: 29/10/2020
4. Part 1-Gene Therapy: A Genetic Counselor’s Perspective

   Pubblicato: 23/10/2020
5. An App to Make Patients the Experts in their Own Conditions

   Pubblicato: 15/10/2020
6. Pursuing a New Target for Autoimmune Diseases

   Pubblicato: 08/10/2020
7. Finding a Rare Friend

   Pubblicato: 02/10/2020
8. Industrializing Individual Therapies for People with Rare Conditions

   Pubblicato: 25/09/2020
9. Rare Disease Advocate Turned Filmmaker Turns Lens on his Son

   Pubblicato: 17/09/2020
10. Inhibiting Signaling that Drives Growth of Rare Malformations

    Pubblicato: 10/09/2020
11. Readying a Rare Disease Community for the Availability of Treatments

    Pubblicato: 03/09/2020
12. Forging a Rare Disease Research Agenda

    Pubblicato: 27/08/2020
13. Delivering Injectable Drugs Orally

    Pubblicato: 20/08/2020
14. What Young Adults with Rare Conditions Need to Know About Health Insurance

    Pubblicato: 14/08/2020
15. Mirum Prepares to Seek Approval for Rare Liver Disease Therapy

    Pubblicato: 07/08/2020
16. Payer Perceptions of Fairness in Pricing Rare Disease Therapies

    Pubblicato: 04/08/2020
17. Improving Narcolepsy Therapy with Drug Delivery Technology

    Pubblicato: 23/07/2020
18. Fighting the Persistent Cough in a Rare and Deadly Lung Disease

    Pubblicato: 15/07/2020
19. Targeting Huntington's Disease with Antisense

    Pubblicato: 08/07/2020
20. Assembling a Pipeline for Rare GI Disorders

    Pubblicato: 01/07/2020