RARECast

548 Episodio

1. Addressing a Shortage of Genetic Counselors with AI

   Pubblicato: 25/04/2024
2. A Small Molecule Therapy to Regenerate Muscle in People with DMD

   Pubblicato: 18/04/2024
3. Forging a Faster Path for Gene Therapies

   Pubblicato: 11/04/2024
4. Determining the Value of Rare Disease Therapies

   Pubblicato: 04/04/2024
5. Buying and Building a Gene Therapy Presence

   Pubblicato: 28/03/2024
6. A Clinical Trial Failure Derails a Promising Technology

   Pubblicato: 21/03/2024
7. Helping People with Undiagnosed Rare Diseases Find Answers

   Pubblicato: 14/03/2024
8. Speeding and Scaling the Development of Genome Editing Therapies

   Pubblicato: 07/03/2024
9. Getting a Next-Generation Genome Editing Therapy for Sickle Cell Disease Back on Track

   Pubblicato: 29/02/2024
10. Trying to Break a Leg in a Wheelchair

    Pubblicato: 22/02/2024
11. A Drug Developer that Makes Pediatric Cancers a Priority

    Pubblicato: 15/02/2024
12. Harnessing the Body’s Natural RNA Machinery to Treat Diseases

    Pubblicato: 08/02/2024
13. Targeting the Leading Cause of Death in Friedreich’s Ataxia with a Gene Therapy

    Pubblicato: 01/02/2024
14. How Inhaled mRNA May Help Rare Disease Patients Breathe Easier

    Pubblicato: 25/01/2024
15. Changing What’s Possible with Cell and Gene Therapies

    Pubblicato: 18/01/2024
16. Why Flying with a Wheelchair Is a Civil Rights Issue

    Pubblicato: 11/01/2024
17. Mapping Spheres of Influence

    Pubblicato: 04/01/2024
18. Bringing Precision to the Treatment of Rare Cancers

    Pubblicato: 28/12/2023
19. The Challenges of Developing a Therapy for Pregnant Women with A Rare Condition

    Pubblicato: 21/12/2023
20. How One Drug Developer Is Addressing Health Inequities

    Pubblicato: 14/12/2023