RARECast

548 Episodio

1. Enabling On-Demand Therapies

   Pubblicato: 16/09/2024
2. After Driving an N-of-1 Therapy for Her Son, an Advocate Turns to Helping Others

   Pubblicato: 05/09/2024
3. Putting Rare Disease Organization in the Business of Drug Development

   Pubblicato: 29/08/2024
4. Understanding the Many Questions Gene Therapies Raise

   Pubblicato: 22/08/2024
5. A Test to Identify People Likely to Develop ALS

   Pubblicato: 15/08/2024
6. How an Ultra-Rare Disease Patient Foundation Advanced a Gene Therapy

   Pubblicato: 08/08/2024
7. Making the $10 Genome a Reality

   Pubblicato: 01/08/2024
8. A No-Nonsense Effort to Develop a Therapy that Works Across Genetic Diseases

   Pubblicato: 25/07/2024
9. Mapping a Perilous Journey with Humor

   Pubblicato: 18/07/2024
10. Restoring Vision in Inherited Retinal Disease

    Pubblicato: 11/07/2024
11. Bringing Genome Sequencing to Rural Populations

    Pubblicato: 04/07/2024
12. Addressing a Blind Spot in Treatments for the Cornea

    Pubblicato: 27/06/2024
13. Taking a Different Approach to Rare Epilepsies

    Pubblicato: 20/06/2024
14. A Rare Disease Drug Developer Tries to Earn Its Stripes

    Pubblicato: 13/06/2024
15. Using Plasma to Treat Rare Diseases

    Pubblicato: 06/06/2024
16. Differentiating Gene Therapies through Regulatory Elements

    Pubblicato: 30/05/2024
17. How One Patient Organization Leverages Research Investments

    Pubblicato: 23/05/2024
18. Charging into the Storm

    Pubblicato: 16/05/2024
19. A Gene Therapy Developer that Embraces Different Models for Reaching Patients

    Pubblicato: 09/05/2024
20. Using Directed Evolution to Develop New Vectors for Genetic Medicines

    Pubblicato: 02/05/2024