RARECast

548 Episodio

1. Bridging the Gap Between Basic and Commercial Research for Rare Disease

   Pubblicato: 26/05/2022
2. Stoking Functional Copies of Genes to Compensate for Mutated Ones

   Pubblicato: 19/05/2022
3. Targeting ALS with Synergistic Combinations of Therapies

   Pubblicato: 13/05/2022
4. How a Polish Rare Disease Organizations Is Helping Its Ukrainian Neighbors

   Pubblicato: 05/05/2022
5. Powering a New Era of Genetic Medicine

   Pubblicato: 28/04/2022
6. Searching for a Diagnosis

   Pubblicato: 21/04/2022
7. A Novel Way to Deliver Rare Disease Therapies

   Pubblicato: 14/04/2022
8. Bringing Diversity, Equity, and Inclusion to the Books We Read

   Pubblicato: 07/04/2022
9. From Mila to Millions: Scaling N of 1 Therapies

   Pubblicato: 31/03/2022
10. Genetically Modifying Patients’ Skin Cells to Treat Rare Diseases

    Pubblicato: 24/03/2022
11. Targeting Rare, Immunologic Disorders

    Pubblicato: 18/03/2022
12. Harnessing a Natural Mechanism to Silence Disease

    Pubblicato: 10/03/2022
13. Advancing Precision Medicine with Patient Data

    Pubblicato: 03/03/2022
14. Pregnancy and Motherhood for a Woman with SMA

    Pubblicato: 24/02/2022
15. Steps to Improve Data Gathering of Rare Diseases

    Pubblicato: 17/02/2022
16. Rare Patients Learn to Make Their Voices Heard

    Pubblicato: 10/02/2022
17. Empowering Patient Organizations with Real-World Data

    Pubblicato: 04/02/2022
18. A Healthcare Communications Student Gets an Education as a Patient

    Pubblicato: 27/01/2022
19. Expanding the CRISPR Toolkit

    Pubblicato: 21/01/2022
20. Marrying Antibodies to RNA Therapies to Target Previously Inaccessible Tissues and Cells

    Pubblicato: 13/01/2022