548 Episodio

  1. Shortening the Diagnostic Odyssey

    Pubblicato: 01/05/2019
  2. Eliminating Barriers to Adoption of Children with Rare Diseases

    Pubblicato: 24/04/2019
  3. A Young Rare Disease Advocate Discusses Life with an Undiagnosed Condition

    Pubblicato: 17/04/2019
  4. The Benefits of an Open-Source Registry for Rare Diseases

    Pubblicato: 10/04/2019
  5. How a Patient Group Helped Drive Drug Development in Rett Syndrome

    Pubblicato: 03/04/2019
  6. How Misperceptions Can Create Barriers to Care

    Pubblicato: 27/03/2019
  7. Targeting Repeat Expansion Disorders with Next-Gen Antisense Drugs

    Pubblicato: 21/03/2019
  8. Getting Misfolding Proteins to Shape Up

    Pubblicato: 13/03/2019
  9. A Different Approach to Inhibiting the Complement System

    Pubblicato: 06/03/2019
  10. Looking Back in Time to Find Rare Disease Patients Today

    Pubblicato: 27/02/2019
  11. Ionis CEO Stanley Crooke Discusses Success as a Platform Technology Company

    Pubblicato: 20/02/2019
  12. Orchard Looks toward Harvesting Expanded Gene Therapy Pipeline

    Pubblicato: 13/02/2019
  13. Connecting Rare Disease Patients in India and the United States

    Pubblicato: 06/02/2019
  14. Regenerative Medicine Moves into the Spotlight

    Pubblicato: 30/01/2019
  15. Learning New Tricks from Pathogenic Bacteria to Target the Microbiome

    Pubblicato: 24/01/2019
  16. Orphan Drug Accelerator Spin-Out Tackles Rare Endocrine Disorders

    Pubblicato: 16/01/2019
  17. Aspa Therapeutics Forges Gene Therapy for Rare Neurological Condition

    Pubblicato: 09/01/2019
  18. How Patient-Led Collaborations Are Transforming Rare Disease Drug Discovery and Development

    Pubblicato: 02/01/2019
  19. Sobi Expands Its Immunology Franchise with HLH Drug Approval

    Pubblicato: 27/12/2018
  20. Learning to Thrive

    Pubblicato: 19/12/2018

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RARECast is a Global Genes podcast hosted by award-winning journalist Daniel Levine. It focuses on the intersection of rare disease with business, science, and policy.

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